Gene

Cell and gene therapy: rewriting the future of medicine

Cell and gene therapy: rewriting the future of medicine

Cell and gene therapies seek to correct the root cause of a disease at the molecular level. These game-changing drugs are reshaping the way we treat previously incurable diseases and transforming people’s lives. Cell and gene therapy represent overlapping areas of research with similar therapeutic goals – to develop a treatment that can correct the …

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Prime Medicine is gearing up for a $200 million IPO.  We dug through the biotech's 282-page dossier to find 5 key points about the company's plan to commercialize gene editing.

Prime Medicine is gearing up for a $200 million IPO. We dug through the biotech’s 282-page dossier to find 5 key points about the company’s plan to commercialize gene editing.

Gene-editing biotech Prime Medicine filed for an IPO on Friday. Prime faces a freezing public market. The number of IPOs in the biotechnology sector decreased by 83% compared to last year. From a key patent to an uncertain timeline, here are five takeaways from Prime’s filing. Prime Medicine seeks to be the first gene-editing biotech …

Prime Medicine is gearing up for a $200 million IPO. We dug through the biotech’s 282-page dossier to find 5 key points about the company’s plan to commercialize gene editing. Read More »

Multimillion-Dollar Gene Therapies Offer Patients Hope, But Huge Cost Problems

Multimillion-Dollar Gene Therapies Offer Patients Hope, But Huge Cost Problems

The era of multimillion-dollar gene therapies has arrived, offering a ray of hope for patients with debilitating diseases – but also presenting enormous accessibility challenges. Why is this important: While the projected number of patients likely to receive the treatments is relatively small, it’s unclear how small employers, state Medicaid programs and the rest of …

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Illustration of nanoparticles with light shining through them

Molecular detection platform offers new insights into gene drug manufacturing

By Gina Wadas / Posted September 23, 2022 An important component of vaccines protecting people against the SARS-CoV-2 virus and its variants are lipid nanoparticles, or LNPs. These circular particles carry therapeutic mRNA payloads, the snippets of genetic material that trigger our immune system’s defense against COVID-19. Even with their success, some characteristics of the …

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Human gene variant in ADHD, autism exposes sex-dependent neural signaling mechanisms

Human gene variant in ADHD, autism exposes sex-dependent neural signaling mechanisms

The prevalence, age of onset, and clinical symptoms of virtually all neuropsychiatric disorders differ between men and women. Disorders with a pronounced gender bias include attention deficit/hyperactivity disorder (ADHD) and autism spectrum disorder (ASD), where the ratio of males to females diagnosed is approximately 4 to 1. If this biased ratio derives from roles played …

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Chroma Medicine Announces Formation of Scientific Advisory Board of Global Experts in Gene Editing and Cell and Gene Therapy

Chroma Medicine Announces Formation of Scientific Advisory Board of Global Experts in Gene Editing and Cell and Gene Therapy

Members Bradley BernsteinMD, Ph.D., Paula Canondoctorate, howard changMD, Ph.D., and Ahmad (Mo) KhalilPh.D., will guide the advancement of the company’s epigenetic editing platform and key programs Scientific Advisors Join Chroma Founders, Luke Gilbertdoctorate, Keith Young MD., Ph.D., David Liudoctorate, Angelo Lombardodoctorate, Luigi NaldiniMD, Ph.D., and jonathan weismanPh.D., expanding the company’s world-class team of genomic medicine …

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